Isocitrate dehydrogenase (IDH) inhibitorFDA-approvedInvestigational

Ivosidenib

How it works

Blocks the IDH2 protein, which is involved in the growth and survival of cancer cells in certain types of leukemia.

Cancer types

LeukemiaIDH1-mutated AML

Efficacy

In clinical trials, around 50% of patients achieved an objective response, with a median overall survival of approximately 10 months.

Side effects

Moderate

Side effects can be significant and may require dose adjustments or supportive medication, but the treatment is usually continued.

Evidence from research

StudyCancer typeStageEfficacy
New Study Examines Ivosidenib and Azacitidine for AML PatientsLeukemiaphase-3Source →
Testing Ivosidenib and Venetoclax for IDH1 Mutated Hematologic MalignanciesLeukemiaphase-1Source →
New Study Compares Effectiveness of Two Leukemia TreatmentsLeukemiaphase-3Treatment with OLU versus IVO was associated with significantly higher rates of complete response (RD: 0.25; 95%CI: 0.01, 0.49), transfusion independence (RD: 0.27; 95%CI: 0.01, 0.53), and OS (HR: 0.33; 95%CI: 0.11, 0.94).Source →
New Study Compares Effectiveness of Leukemia TreatmentsLeukemiameta-analysisSource →

This information is provided for general education only and is not medical advice. Always consult a qualified healthcare professional before making treatment decisions.