Tyrosine kinase inhibitorFDA-approvedInvestigational

Ponatinib

How it works

Blocks the BCR-ABL tyrosine kinase enzyme, which is overactive in CML cells, and also inhibits other tyrosine kinases involved in cancer growth.

Cancer types

LeukemiaBCR-ABL-positive

Efficacy

In clinical trials, around 50% of BCR-ABL-positive patients achieved a major cytogenetic response, with a median progression-free survival of approximately 1 year.

Side effects

Severe

This treatment carries a higher risk of serious side effects. Close medical monitoring is required throughout treatment.

Evidence from research

StudyCancer typeStageEfficacy
Asciminib Study for CML Patients Resistant to PonatinibLeukemiaphase-2Source →
Combination Chemotherapy and Ponatinib Hydrochloride in Treating Acute Lymphoblastic LeukemiaLeukemiaphase-2Source →
Testing Combination Therapy for CD22-Positive B-Lineage Acute Lymphoblastic LeukemiaLeukemiaphase-2Source →
Evaluating Ponatinib Hydrochloride for Chronic Myeloid LeukemiaLeukemiaphase-2Source →
Combining Ponatinib and Vitamin K2 May Help Treat Acute Myeloid LeukemiaLeukemialab-studySource →
Choosing the Right Second-Line Treatment for Chronic Myeloid LeukemiaLeukemiareviewSource →
Ponatinib Improves Quality of Life for Leukemia PatientsLeukemiaphase-3Source →
Ponatinib-based therapy shows promise for CML in myeloid blast phaseLeukemiaphase-2The rate of morphological remission with or without count recovery (i.e. overall response rate [ORR]) was 49%.Source →
Combining Two Leukemia Treatments Shows Promise in Lab ExperimentsLeukemialab-studySource →
Combining Ponatinib and Blinatumomab in Leukemia TreatmentLeukemiaphase-2The complete molecular response rate was 83% and the rate of measurable residual disease negativity was 98%.Source →
BCR::ABL1 Inhibitors Affect Blood Vessel Growth DifferentlyLeukemialab-studySource →
New Study Compares Treatments for a Specific Type of LeukaemiaLeukemiaphase-3Source →
Ponatinib's Long-Term Effects in Chronic Myeloid Leukemia PatientsLeukemiaobservationalThe estimated 2-year progression-free survival was 84%.Source →
Comparing Ponatinib Doses for Chronic Myeloid LeukemiaLeukemiameta-analysis45 mg ponatinib was superior to other doses of ponatinib and other TKIs in CCyR, MCyR and CHR.Source →
Ponatinib vs Imatinib for Leukemia Treatment: Cost ComparisonLeukemiaphase-3Ponatinib offered an approximate gain of 3 months of life and 6 months of quality-adjusted life.Source →

This information is provided for general education only and is not medical advice. Always consult a qualified healthcare professional before making treatment decisions.